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Alpha-1 Antitrypsin Deficiency (2 companies)
Companies with an active program in Alpha-1 Antitrypsin Deficiency.
| Ticker | Company | Therapeutic areas | Programs | Lead stage | Programs |
|---|---|---|---|---|---|
| BEAM | Beam Therapeutics Inc. | HematologyMetabolicRespiratory Rare | 1 | Phase 1 | 8 |
| WVE | Wave Life Sciences Ltd. | MetabolicNeurologyRespiratory Rare | 1 | Phase 2 | 5 |
No companies match.