Voyager Therapeutics, Inc. VYGR
- glucosylceramidase beta 1 gene therapy — Gaucher Disease Preclinical
- glucosylceramidase beta 1 gene therapy — Parkinson's Disease Preclinical
GBA1 (2 companies · 3 programs)
Companies with an active program directed at GBA1.
Gain Therapeutics, Inc. GANX
- GT-02287 — Parkinson's Disease Phase 1