IONIS PHARMACEUTICALS INC IONS
- tominersen — Huntington's Disease Phase 1
HTT (4 companies · 4 programs)
Companies with an active program directed at HTT.
Sarepta Therapeutics, Inc. SRPT
- HTT siRNA — Huntington's Disease Preclinical
uniQure N.V. QURE
- ifezuntirgene inilparvovec — Huntington's Disease NDA Submitted
Wave Life Sciences Ltd. WVE
- WVE-003 — Huntington's Disease Phase 1