Neurogene Inc. NGNE
- NGN-401 — Rett Syndrome Phase 3
MECP2 (3 companies · 3 programs)
Companies with an active program directed at MECP2.
ProQR Therapeutics N.V. PRQR
- AX-2402 — Rett Syndrome Preclinical
Taysha Gene Therapies, Inc. TSHA
- TSHA-102 — Rett Syndrome Phase 3