Home › Targets › TTR
TTR (2 companies · 6 programs)
Companies with an active program directed at TTR.
- WAINUA — Hereditary Transthyretin-Mediated Amyloid Polyneuropathy Approved
- WAINUA — Transthyretin-Mediated Amyloid Cardiomyopathy Phase 3
- TEGSEDI — Hereditary Transthyretin-Mediated Amyloid Polyneuropathy Approved
- WAINUA — Transthyretin Amyloid Cardiomyopathy Phase 3
- nexiguran ziclumeran — Transthyretin Amyloidosis with Cardiomyopathy Phase 3
- nexiguran ziclumeran — Hereditary Transthyretin Amyloidosis with Polyneuropathy Phase 3