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Classical Homocystinuria (2 companies)

Companies with an active program in Classical Homocystinuria.

Ticker Company Therapeutic areas Programs Lead stage Programs
ETON Eton Pharmaceuticals, Inc. GI/HepatologyMetabolicRenal Rare 1 Approved 14
TVTX Travere Therapeutics, Inc. MetabolicRenal Rare 1 Approved 4