Metabolic (46 companies · 43 conditions)

Conditions

Obesity 10 Type 1 Diabetes 9 Type 2 Diabetes 8 MASH 7 Prader-Willi Syndrome 4 Rare Gout 3 Adrenal Insufficiency 2 Bardet-Biedl Syndrome 2 Rare Classical Homocystinuria 2 Rare Congenital Adrenal Hyperplasia 2 Rare Cushing's Syndrome 2 Rare Gaucher Disease 2 Rare Glycogen Storage Disease Type Ia 2 Rare Phenylketonuria 2 Rare Pompe Disease 2 Rare Urea Cycle Disorders 2 Rare Achondroplasia 1 Rare Acromegaly 1 Rare Aging-Related Frailty 1 Choline Deficiency 1 Congenital Hyperinsulinism 1 Rare Fabry Disease 1 Rare Hyperammonemia 1 Rare Hypoparathyroidism 1 Rare Hypothyroidism 1 Lipodystrophy 1 Rare Long-Chain Fatty Acid Oxidation Disorders 1 Rare Menkes Disease 1 Rare Mitochondrial Disease 1 Rare MPS I 1 Rare Mucopolysaccharidosis Type IIIB 1 Rare Mucopolysaccharidosis Type VII 1 Rare Neonatal Diabetes Mellitus 1 Rare Osteogenesis Imperfecta 1 Rare Osteoporosis 1 Post-Bariatric Hypoglycemia 1 Rare Sanfilippo Syndrome 1 Rare Severe Hypoglycemia 1 Severe Primary IGF-1 Deficiency 1 Rare Tumor-Induced Osteomalacia 1 Rare Tyrosinemia Type 1 1 Rare Wolfram Syndrome 1 Rare X-Linked Hypophosphatemia 1 Rare

Companies

Ticker	Company	Therapeutic areas	In Metabolic	Lead stage	Programs
ALT	Altimmune	GI/HepatologyMetabolic+1	1	Phase 3	3
AMLX	Amylyx Pharmaceuticals	MetabolicNeurology Rare	4	Phase 3	5
BEAM	Beam Therapeutics	HematologyMetabolic+1 Rare	2	Phase 2	6
BLTE	Belite Bio	MetabolicOphthalmology Rare	4	NDA Submitted	6
BMEA	Biomea Fusion	MetabolicOncology	3	Phase 2	4
IPSC	Century Therapeutics	ImmunologyMetabolic+1 Rare	1	Phase 1	9
CMMB	Chemomab Therapeutics	GI/HepatologyImmunology+1 Rare	1	Phase 2	4
CRNX	Crinetics Pharmaceuticals	MetabolicOncology Rare	4	Approved	6
DYN	Dyne Therapeutics	MetabolicNeurology Rare	1	NDA Submitted	10
ELDN	Eledon Pharmaceuticals	ImmunologyMetabolic+1 Rare	1	Phase 2	3
ENTX	Entera Bio	GI/HepatologyMetabolic Rare	3	Phase 2	4
ETON	Eton Pharmaceuticals	GI/HepatologyInfectious Disease+2 Rare	8	Approved	14
FBIO	Fortress Biotech	DermatologyHematology+2 Rare	3	Approved	12
GUTS	Fractyl Health	Metabolic	3	Phase 3	3
GANX	Gain Therapeutics	MetabolicNeurology Rare	1	Phase 1	5
HRMY	Harmony Biosciences	MetabolicNeurology Rare	2	Approved	17
IMCR	Immunocore	DermatologyInfectious Disease+2	1	Approved	11
IONS	Ionis Pharmaceuticals	CardiovascularHematology+5 Rare	1	Approved	29
KURA	Kura Oncology	MetabolicOncology	2	Approved	12
LCTX	Lineage Cell Therapeutics	MetabolicNeurology+1 Rare	1	Phase 2	12
LGVN	Longeveron	CardiovascularMetabolic+1 Rare	1	Phase 2	4
MGTX	MeiraGTx	ImmunologyMetabolic+2 Rare	3	Phase 2	16
GLUE	Monte Rosa Therapeutics	CardiovascularDermatology+3 Rare	1	Phase 2	7
NKTR	Nektar Therapeutics	DermatologyImmunology+2	1	Phase 3	11
NAMS	NewAmsterdam Pharma	CardiovascularMetabolic+1	1	NDA Submitted	6
PTN	Palatin Technologies	ImmunologyMetabolic+1 Rare	4	Phase 3	8
DTIL	Precision Biosciences	Infectious DiseaseMetabolic+1 Rare	2	Phase 1	5
PRQR	ProQR Therapeutics	MetabolicNeurology Rare	2	Phase 1	7
PTGX	Protagonist Therapeutics	DermatologyHematology+1 Rare	4	Approved	11
TARA	Protara Therapeutics	DermatologyMetabolic+1 Rare	1	Phase 3	3
RLMD	Relmada Therapeutics	MetabolicNeurology+1 Rare	1	Phase 2	4
RYTM	Rhythm Pharmaceuticals	Metabolic Rare	13	Approved	13
SABS	SAB Biotherapeutics	Metabolic	1	Phase 2	1
SGMT	Sagimet Biosciences	DermatologyMetabolic	1	NDA Submitted	3
SANA	Sana Biotechnology	MetabolicOncology	2	Phase 1	4
SPRB	Spruce Biosciences	Metabolic Rare	2	Preclinical	2
GPCR	Structure Therapeutics	MetabolicRespiratory Rare	4	Phase 3	5
TVTX	Travere Therapeutics	MetabolicRenal Rare	1	Approved	7
TYRA	Tyra Biosciences	MetabolicOncology Rare	1	Phase 2	5
RARE	Ultragenyx Pharmaceutical	CardiovascularGI/Hepatology+2 Rare	8	Approved	12
QURE	uniQure	HematologyMetabolic+1 Rare	1	Approved	4
VKTX	Viking Therapeutics	MetabolicNeurology Rare	5	Phase 3	8
VYGR	Voyager Therapeutics	MetabolicNeurology Rare	1	Phase 1	9
VTVT	vTv Therapeutics	MetabolicRespiratory Rare	4	Phase 3	8
WVE	Wave Life Sciences	MetabolicNeurology+1 Rare	2	Phase 2	5
XERS	Xeris Biopharma	MetabolicNeurology Rare	3	Approved	4