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Sanfilippo Syndrome (1 companies)
Companies with an active program in Sanfilippo Syndrome.
| Ticker | Company | Therapeutic areas | Programs | Lead stage | Programs |
|---|---|---|---|---|---|
| RARE | Ultragenyx Pharmaceutical Inc. | CardiovascularGI/HepatologyMetabolicNeurology Rare | 1 | Approved | 12 |
No companies match.