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Urea Cycle Disorders (2 companies)

Companies with an active program in Urea Cycle Disorders.

Ticker Company Therapeutic areas Programs Lead stage Programs
DTIL Precision Biosciences Infectious DiseaseMetabolic+1 Rare 1 Phase 1 4
RARE Ultragenyx Pharmaceutical CardiovascularGI/Hepatology+2 Rare 1 Approved 12