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Amyotrophic Lateral Sclerosis (13 companies)

Companies with an active program in Amyotrophic Lateral Sclerosis.

Ticker Company Therapeutic areas Programs Lead stage Programs
AMLX Amylyx Pharmaceuticals MetabolicNeurology Rare 1 Phase 3 5
ANNX Annexon HematologyNeurology+2 Rare 1 Phase 3 6
CRVO CervoMed Neurology Rare 1 Phase 2 4
CLNN Clene Neurology Rare 1 Phase 3 5
ELDN Eledon Pharmaceuticals ImmunologyMetabolic+1 Rare 1 Phase 2 3
INSM Insmed CardiovascularImmunology+2 Rare 1 Approved 17
IONS Ionis Pharmaceuticals CardiovascularHematology+5 Rare 3 Approved 29
MGTX MeiraGTx ImmunologyMetabolic+2 Rare 1 Phase 2 16
NRSN NeuroSense Therapeutics Neurology Rare 1 Phase 2 3
NRXP NRX Pharmaceuticals Neurology Rare 1 NDA Submitted 6
KTTA Pasithea Therapeutics NeurologyOncology Rare 1 Phase 1 4
PMN ProMIS Neurosciences Neurology Rare 1 Phase 1 6
VYGR Voyager Therapeutics MetabolicNeurology Rare 2 Phase 1 9