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Friedreich's Ataxia (4 companies)

Companies with an active program in Friedreich's Ataxia.

Ticker Company Therapeutic areas Programs Lead stage Programs
LRMR Larimar Therapeutics, Inc. Neurology Rare 1 Phase 3 1
LXEO Lexeo Therapeutics, Inc. CardiovascularNeurology Rare 1 Phase 1 10
SLDB Solid Biosciences Inc. CardiovascularNeurology Rare 1 Phase 3 6
VYGR Voyager Therapeutics, Inc. MetabolicNeurology Rare 1 Phase 1 7