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Huntington's Disease (3 companies)

Companies with an active program in Huntington's Disease.

Ticker Company Therapeutic areas Programs Lead stage Programs
ANNX Annexon, Inc. HematologyNeurologyOphthalmologyRenal Rare 1 NDA Submitted 6
QURE uniQure N.V. HematologyMetabolicNeurology Rare 1 Approved 6
WVE Wave Life Sciences Ltd. MetabolicNeurologyRespiratory Rare 1 Phase 2 5