Home › Therapeutic areas › Neurology › Myotonic Dystrophy
Myotonic Dystrophy (4 companies)
Companies with an active program in Myotonic Dystrophy.
| Ticker | Company | Therapeutic areas | Programs | Lead stage | Programs |
|---|---|---|---|---|---|
| DYN | Dyne Therapeutics | MetabolicNeurology Rare | 1 | NDA Submitted | 10 |
| HRMY | Harmony Biosciences | MetabolicNeurology Rare | 1 | Approved | 17 |
| PEPG | PepGen | Neurology Rare | 1 | Phase 2 | 1 |
| SRPT | Sarepta Therapeutics | NeurologyRespiratory Rare | 1 | Approved | 10 |
No companies match.