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133 clinical-stage companies. Search or filter to narrow the list.

Ticker Company Therapeutic areas Lead stage Programs
ABSI Absci Corporation DermatologyGI/HepatologyWomen's Health Phase 1 7
ACRS Aclaris Therapeutics DermatologyRespiratory Phase 2 7
ACRV Acrivon Therapeutics Oncology Phase 2 5
ACTU Actuate Therapeutics Oncology Phase 2 7
ABOS Acumen Pharmaceuticals Neurology Phase 2 2
ADAG Adagene Inc. Oncology Phase 2 9
AKBA Akebia Therapeutics, Inc. HematologyOphthalmologyRenalRespiratory Rare Approved 14
AKTS Aktis Oncology, Inc. Oncology Phase 1 9
ALDX Aldeyra Therapeutics, Inc. DermatologyOncologyOphthalmology Rare NDA Submitted 8
ALLO Allogene Therapeutics, Inc. ImmunologyOncology Rare Phase 2 12
DRTS Alpha Tau Medical Ltd. Oncology Phase 2 5
ATHE ALTERITY THERAPEUTICS LTD Neurology Rare Phase 2 2
ALT Altimmune, Inc. GI/HepatologyMetabolicNeurology Phase 2 3
AMLX Amylyx Pharmaceuticals, Inc. MetabolicNeurology Rare Phase 3 5
ANAB ANAPTYSBIO, INC DermatologyGI/HepatologyImmunologyOncology Rare Approved 6
ANNX Annexon, Inc. HematologyNeurologyOphthalmologyRenal Rare NDA Submitted 6
APGE Apogee Therapeutics, Inc. DermatologyRespiratory Phase 2 8
RCUS Arcus Biosciences, Inc. DermatologyImmunologyOncology Phase 3 7
ARTV Artiva Biotherapeutics, Inc. DermatologyImmunologyOncologyRenal Rare Phase 2 16
ARVN ARVINAS, INC. NeurologyOncology Rare Approved 15
ATAI AtaiBeckley Inc. Neurology Phase 3 5
BEAM Beam Therapeutics Inc. HematologyMetabolicRespiratory Rare Phase 1 8
BIOA BioAge Labs, Inc. CardiovascularMetabolicOphthalmology Phase 1 2
BMEA Biomea Fusion, Inc. Metabolic Phase 2 4
BCTX BriaCell Therapeutics Corp. Oncology Phase 3 8
BBOT BridgeBio Oncology Therapeutics, Inc. Oncology Phase 1 8
CCCC C4 Therapeutics, Inc. Oncology Phase 2 2
CABA Cabaletta Bio, Inc. DermatologyImmunologyNeurologyRenal Rare Phase 1 8
CRDL Cardiol Therapeutics Inc. Cardiovascular Rare Phase 3 4
CRBU Caribou Biosciences, Inc. ImmunologyOncology Phase 3 4
CLDX Celldex Therapeutics, Inc. DermatologyGI/HepatologyImmunologyRespiratory Phase 3 7
CLRB Cellectar Biosciences, Inc. Oncology NDA Submitted 11
IPSC Century Therapeutics, Inc. ImmunologyMetabolicRenal Rare Phase 1 11
CRVO CervoMed Inc. Neurology Rare Phase 2 5
CGON CG Oncology, Inc. Oncology NDA Submitted 1
CING Cingulate Inc. 1
CLNN Clene Inc. Neurology Rare NDA Submitted 5
CLYM Climb Bio, Inc. HematologyImmunologyRenal Rare Phase 2 7
COGT Cogent Biosciences, Inc. HematologyOncology Rare NDA Submitted 7
CGTX COGNITION THERAPEUTICS INC NeurologyOphthalmology Phase 2 2
CHRS Coherus Oncology, Inc. Oncology Approved 4
CMPS COMPASS Pathways plc Neurology NDA Submitted 3
CRVS Corvus Pharmaceuticals, Inc. DermatologyOncology Phase 3 4
CBIO CRESCENT BIOPHARMA, INC. Oncology Phase 1 10
CRNX Crinetics Pharmaceuticals, Inc. MetabolicOncology Rare Approved 7
CUE Cue Biopharma, Inc. Preclinical 4
CGEM Cullinan Therapeutics, Inc. ImmunologyOncology NDA Submitted 7
HELP CYBIN INC. Neurology Phase 2 4
CYDY CytoDyn Inc. Oncology Phase 2 2
CTMX CytomX Therapeutics, Inc. Oncology Phase 1 3
DBVT DBV Technologies S.A. GI/HepatologyImmunology Rare NDA Submitted 3
DFTX Definium Therapeutics, Inc. Neurology Phase 3 4
DYN Dyne Therapeutics, Inc. MetabolicNeurology Rare Phase 3 10
ENTA ENANTA PHARMACEUTICALS INC DermatologyImmunologyInfectious Disease Phase 2 6
ERAS Erasca, Inc. Oncology Phase 1 4
ETON Eton Pharmaceuticals, Inc. GI/HepatologyMetabolicRenal Rare Approved 14
EVMN Evommune, Inc. DermatologyImmunologyNeurology Phase 2 6
EXEL EXELIXIS, INC. Oncology NDA Submitted 2
EYPT EyePoint, Inc. Ophthalmology Phase 3 3
FBRX Forte Biosciences, Inc. DermatologyGI/Hepatology Phase 2 3
FBIO Fortress Biotech, Inc. DermatologyHematologyMetabolic Rare Approved 14
GUTS FRACTYL HEALTH, INC. Metabolic Phase 3 3
GANX Gain Therapeutics, Inc. MetabolicNeurology Rare Phase 1 5
GHRS GH Research PLC NeurologyWomen's Health Phase 2 4
GOSS Gossamer Bio, Inc. Cardiovascular Rare Phase 3 6
GRCE Grace Therapeutics, Inc. Neurology Rare Phase 3 3
GLSI Greenwich LifeSciences, Inc. Oncology Phase 3 1
IMTX Immatics N.V. Oncology Phase 2 8
IMMX Immix Biopharma, Inc. Hematology Rare Phase 2 1
IMRX Immuneering Corp Oncology Phase 3 5
IBRX ImmunityBio, Inc. Infectious DiseaseOncology Approved 17
IMVT Immunovant, Inc. ImmunologyNeurology Rare Phase 2 6
INAB IN8BIO, INC. ImmunologyOncology Phase 2 6
IXHL Incannex Healthcare Inc. ImmunologyNeurologyRespiratory Phase 2 3
NTLA Intellia Therapeutics, Inc. CardiovascularImmunology Rare NDA Submitted 5
JBIO Jade Biosciences, Inc. ImmunologyRenal Rare Phase 1 5
JANX Janux Therapeutics, Inc. Oncology Phase 1 3
KPRX KIORA PHARMACEUTICALS INC Ophthalmology Rare Phase 2 5
KOD Kodiak Sciences Inc. Ophthalmology Phase 3 7
KURA Kura Oncology, Inc. MetabolicOncology Phase 1 9
KYMR Kymera Therapeutics, Inc. DermatologyRespiratory Phase 2 5
KYTX Kyverna Therapeutics, Inc. ImmunologyNeurologyRenal Rare NDA Submitted 7
LRMR Larimar Therapeutics, Inc. Neurology Rare Phase 3 1
LXEO Lexeo Therapeutics, Inc. CardiovascularNeurology Rare Phase 1 10
LGVN Longeveron Inc. CardiovascularMetabolicNeurology Rare Phase 2 4
MAIA MAIA Biotechnology, Inc. Oncology Phase 2 7
MRKR Marker Therapeutics, Inc. Oncology Phase 1 4
MDNAF Medicenna Therapeutics Corp. Oncology Phase 2 9
MIST Milestone Pharmaceuticals Inc. Cardiovascular Phase 3 3
GLUE Monte Rosa Therapeutics, Inc. CardiovascularDermatologyMetabolicOncology Rare Phase 1 8
NGEN NERVGEN PHARMA CORP. Neurology Preclinical 2
NRXP NRX Pharmaceuticals, Inc. Neurology NDA Submitted 5
NRIX Nurix Therapeutics, Inc. Oncology Phase 2 13
OCGN Ocugen, Inc. Infectious DiseaseOphthalmology Rare Phase 3 13
OMER OMEROS CORP HematologyNeurologyOncologyRespiratory Rare NDA Submitted 7
ORKA Oruka Therapeutics, Inc. DermatologyImmunology Rare Phase 2 6
OVID Ovid Therapeutics Inc. Neurology Rare Phase 1 6
KTTA Pasithea Therapeutics Corp. NeurologyOncology Phase 1 3
CATX Perspective Therapeutics, Inc. Oncology Phase 1 3
PHIO Phio Pharmaceuticals Corp. Oncology Phase 1 4
PMVP PMV Pharmaceuticals, Inc. Oncology Phase 2 7
PCSA Processa Pharmaceuticals, Inc. GI/HepatologyOncologyRenal Rare Phase 2 8
TARA Protara Therapeutics, Inc. DermatologyMetabolicOncology Rare Phase 3 3
REPL Replimune Group, Inc. Oncology Phase 3 4
RVPH REVIVA PHARMACEUTICALS HOLDINGS, INC. CardiovascularDermatologyNeurologyRespiratory Rare Phase 3 10
RYTM RHYTHM PHARMACEUTICALS, INC. Metabolic Rare Approved 13
RCKT ROCKET PHARMACEUTICALS, INC. CardiovascularHematologyImmunology Rare Approved 4
SGMT Sagimet Biosciences Inc. DermatologyMetabolic Phase 3 5
SANA Sana Biotechnology, Inc. MetabolicOncology Phase 1 5
SRPT Sarepta Therapeutics, Inc. Neurology Rare Approved 10
SLS SELLAS Life Sciences Group, Inc. Oncology Phase 3 8
SLDB Solid Biosciences Inc. CardiovascularNeurology Rare Phase 3 6
SPRB SPRUCE BIOSCIENCES, INC. MetabolicNeurology Rare Preclinical 2
SYRE Spyre Therapeutics, Inc. Immunology Phase 2 12
GPCR Structure Therapeutics Inc. MetabolicRespiratory Rare Phase 2 5
SMMT Summit Therapeutics Inc. Oncology Phase 3 3
STRO SUTRO BIOPHARMA, INC. Oncology Phase 1 5
TNGX Tango Therapeutics, Inc. Oncology Phase 1 6
TSHA Taysha Gene Therapies, Inc. Neurology Rare Phase 3 3
TVTX Travere Therapeutics, Inc. MetabolicRenal Rare Approved 4
TTRX Turn Therapeutics Inc. DermatologyInfectious Disease Phase 2 4
RARE Ultragenyx Pharmaceutical Inc. CardiovascularGI/HepatologyMetabolicNeurology Rare Approved 12
QURE uniQure N.V. HematologyMetabolicNeurology Rare Approved 6
VNDA Vanda Pharmaceuticals Inc. CardiovascularDermatologyGI/HepatologyHematologyImmunologyInfectious DiseaseNeurologyOphthalmology Rare Approved 26
VERA Vera Therapeutics, Inc. Infectious DiseaseRenal Rare NDA Submitted 8
VKTX Viking Therapeutics, Inc. GI/HepatologyMetabolicNeurology Rare Phase 3 9
VIR Vir Biotechnology, Inc. Infectious DiseaseOncology Rare Phase 3 10
VRDN Viridian Therapeutics, Inc.\DE Ophthalmology NDA Submitted 6
VOR Vor Biopharma Inc. ImmunologyNeurologyOncology Rare Phase 3 4
VYGR Voyager Therapeutics, Inc. MetabolicNeurology Rare Phase 1 7
VTVT vTv Therapeutics Inc. MetabolicRespiratory Rare Phase 3 8
WVE Wave Life Sciences Ltd. MetabolicNeurologyRespiratory Rare Phase 2 5
XENE Xenon Pharmaceuticals Inc. Neurology Phase 3 9