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133 clinical-stage companies. Search or filter to narrow the list.
| Ticker | Company | Therapeutic areas | Lead stage | Programs |
|---|---|---|---|---|
| ABSI | Absci Corporation | DermatologyGI/HepatologyWomen's Health | Phase 1 | 7 |
| ACRS | Aclaris Therapeutics | DermatologyRespiratory | Phase 2 | 7 |
| ACRV | Acrivon Therapeutics | Oncology | Phase 2 | 5 |
| ACTU | Actuate Therapeutics | Oncology | Phase 2 | 7 |
| ABOS | Acumen Pharmaceuticals | Neurology | Phase 2 | 2 |
| ADAG | Adagene Inc. | Oncology | Phase 2 | 9 |
| AKBA | Akebia Therapeutics, Inc. | HematologyOphthalmologyRenalRespiratory Rare | Approved | 14 |
| AKTS | Aktis Oncology, Inc. | Oncology | Phase 1 | 9 |
| ALDX | Aldeyra Therapeutics, Inc. | DermatologyOncologyOphthalmology Rare | NDA Submitted | 8 |
| ALLO | Allogene Therapeutics, Inc. | ImmunologyOncology Rare | Phase 2 | 12 |
| DRTS | Alpha Tau Medical Ltd. | Oncology | Phase 2 | 5 |
| ATHE | ALTERITY THERAPEUTICS LTD | Neurology Rare | Phase 2 | 2 |
| ALT | Altimmune, Inc. | GI/HepatologyMetabolicNeurology | Phase 2 | 3 |
| AMLX | Amylyx Pharmaceuticals, Inc. | MetabolicNeurology Rare | Phase 3 | 5 |
| ANAB | ANAPTYSBIO, INC | DermatologyGI/HepatologyImmunologyOncology Rare | Approved | 6 |
| ANNX | Annexon, Inc. | HematologyNeurologyOphthalmologyRenal Rare | NDA Submitted | 6 |
| APGE | Apogee Therapeutics, Inc. | DermatologyRespiratory | Phase 2 | 8 |
| RCUS | Arcus Biosciences, Inc. | DermatologyImmunologyOncology | Phase 3 | 7 |
| ARTV | Artiva Biotherapeutics, Inc. | DermatologyImmunologyOncologyRenal Rare | Phase 2 | 16 |
| ARVN | ARVINAS, INC. | NeurologyOncology Rare | Approved | 15 |
| ATAI | AtaiBeckley Inc. | Neurology | Phase 3 | 5 |
| BEAM | Beam Therapeutics Inc. | HematologyMetabolicRespiratory Rare | Phase 1 | 8 |
| BIOA | BioAge Labs, Inc. | CardiovascularMetabolicOphthalmology | Phase 1 | 2 |
| BMEA | Biomea Fusion, Inc. | Metabolic | Phase 2 | 4 |
| BCTX | BriaCell Therapeutics Corp. | Oncology | Phase 3 | 8 |
| BBOT | BridgeBio Oncology Therapeutics, Inc. | Oncology | Phase 1 | 8 |
| CCCC | C4 Therapeutics, Inc. | Oncology | Phase 2 | 2 |
| CABA | Cabaletta Bio, Inc. | DermatologyImmunologyNeurologyRenal Rare | Phase 1 | 8 |
| CRDL | Cardiol Therapeutics Inc. | Cardiovascular Rare | Phase 3 | 4 |
| CRBU | Caribou Biosciences, Inc. | ImmunologyOncology | Phase 3 | 4 |
| CLDX | Celldex Therapeutics, Inc. | DermatologyGI/HepatologyImmunologyRespiratory | Phase 3 | 7 |
| CLRB | Cellectar Biosciences, Inc. | Oncology | NDA Submitted | 11 |
| IPSC | Century Therapeutics, Inc. | ImmunologyMetabolicRenal Rare | Phase 1 | 11 |
| CRVO | CervoMed Inc. | Neurology Rare | Phase 2 | 5 |
| CGON | CG Oncology, Inc. | Oncology | NDA Submitted | 1 |
| CING | Cingulate Inc. | — | — | 1 |
| CLNN | Clene Inc. | Neurology Rare | NDA Submitted | 5 |
| CLYM | Climb Bio, Inc. | HematologyImmunologyRenal Rare | Phase 2 | 7 |
| COGT | Cogent Biosciences, Inc. | HematologyOncology Rare | NDA Submitted | 7 |
| CGTX | COGNITION THERAPEUTICS INC | NeurologyOphthalmology | Phase 2 | 2 |
| CHRS | Coherus Oncology, Inc. | Oncology | Approved | 4 |
| CMPS | COMPASS Pathways plc | Neurology | NDA Submitted | 3 |
| CRVS | Corvus Pharmaceuticals, Inc. | DermatologyOncology | Phase 3 | 4 |
| CBIO | CRESCENT BIOPHARMA, INC. | Oncology | Phase 1 | 10 |
| CRNX | Crinetics Pharmaceuticals, Inc. | MetabolicOncology Rare | Approved | 7 |
| CUE | Cue Biopharma, Inc. | — | Preclinical | 4 |
| CGEM | Cullinan Therapeutics, Inc. | ImmunologyOncology | NDA Submitted | 7 |
| HELP | CYBIN INC. | Neurology | Phase 2 | 4 |
| CYDY | CytoDyn Inc. | Oncology | Phase 2 | 2 |
| CTMX | CytomX Therapeutics, Inc. | Oncology | Phase 1 | 3 |
| DBVT | DBV Technologies S.A. | GI/HepatologyImmunology Rare | NDA Submitted | 3 |
| DFTX | Definium Therapeutics, Inc. | Neurology | Phase 3 | 4 |
| DYN | Dyne Therapeutics, Inc. | MetabolicNeurology Rare | Phase 3 | 10 |
| ENTA | ENANTA PHARMACEUTICALS INC | DermatologyImmunologyInfectious Disease | Phase 2 | 6 |
| ERAS | Erasca, Inc. | Oncology | Phase 1 | 4 |
| ETON | Eton Pharmaceuticals, Inc. | GI/HepatologyMetabolicRenal Rare | Approved | 14 |
| EVMN | Evommune, Inc. | DermatologyImmunologyNeurology | Phase 2 | 6 |
| EXEL | EXELIXIS, INC. | Oncology | NDA Submitted | 2 |
| EYPT | EyePoint, Inc. | Ophthalmology | Phase 3 | 3 |
| FBRX | Forte Biosciences, Inc. | DermatologyGI/Hepatology | Phase 2 | 3 |
| FBIO | Fortress Biotech, Inc. | DermatologyHematologyMetabolic Rare | Approved | 14 |
| GUTS | FRACTYL HEALTH, INC. | Metabolic | Phase 3 | 3 |
| GANX | Gain Therapeutics, Inc. | MetabolicNeurology Rare | Phase 1 | 5 |
| GHRS | GH Research PLC | NeurologyWomen's Health | Phase 2 | 4 |
| GOSS | Gossamer Bio, Inc. | Cardiovascular Rare | Phase 3 | 6 |
| GRCE | Grace Therapeutics, Inc. | Neurology Rare | Phase 3 | 3 |
| GLSI | Greenwich LifeSciences, Inc. | Oncology | Phase 3 | 1 |
| IMTX | Immatics N.V. | Oncology | Phase 2 | 8 |
| IMMX | Immix Biopharma, Inc. | Hematology Rare | Phase 2 | 1 |
| IMRX | Immuneering Corp | Oncology | Phase 3 | 5 |
| IBRX | ImmunityBio, Inc. | Infectious DiseaseOncology | Approved | 17 |
| IMVT | Immunovant, Inc. | ImmunologyNeurology Rare | Phase 2 | 6 |
| INAB | IN8BIO, INC. | ImmunologyOncology | Phase 2 | 6 |
| IXHL | Incannex Healthcare Inc. | ImmunologyNeurologyRespiratory | Phase 2 | 3 |
| NTLA | Intellia Therapeutics, Inc. | CardiovascularImmunology Rare | NDA Submitted | 5 |
| JBIO | Jade Biosciences, Inc. | ImmunologyRenal Rare | Phase 1 | 5 |
| JANX | Janux Therapeutics, Inc. | Oncology | Phase 1 | 3 |
| KPRX | KIORA PHARMACEUTICALS INC | Ophthalmology Rare | Phase 2 | 5 |
| KOD | Kodiak Sciences Inc. | Ophthalmology | Phase 3 | 7 |
| KURA | Kura Oncology, Inc. | MetabolicOncology | Phase 1 | 9 |
| KYMR | Kymera Therapeutics, Inc. | DermatologyRespiratory | Phase 2 | 5 |
| KYTX | Kyverna Therapeutics, Inc. | ImmunologyNeurologyRenal Rare | NDA Submitted | 7 |
| LRMR | Larimar Therapeutics, Inc. | Neurology Rare | Phase 3 | 1 |
| LXEO | Lexeo Therapeutics, Inc. | CardiovascularNeurology Rare | Phase 1 | 10 |
| LGVN | Longeveron Inc. | CardiovascularMetabolicNeurology Rare | Phase 2 | 4 |
| MAIA | MAIA Biotechnology, Inc. | Oncology | Phase 2 | 7 |
| MRKR | Marker Therapeutics, Inc. | Oncology | Phase 1 | 4 |
| MDNAF | Medicenna Therapeutics Corp. | Oncology | Phase 2 | 9 |
| MIST | Milestone Pharmaceuticals Inc. | Cardiovascular | Phase 3 | 3 |
| GLUE | Monte Rosa Therapeutics, Inc. | CardiovascularDermatologyMetabolicOncology Rare | Phase 1 | 8 |
| NGEN | NERVGEN PHARMA CORP. | Neurology | Preclinical | 2 |
| NRXP | NRX Pharmaceuticals, Inc. | Neurology | NDA Submitted | 5 |
| NRIX | Nurix Therapeutics, Inc. | Oncology | Phase 2 | 13 |
| OCGN | Ocugen, Inc. | Infectious DiseaseOphthalmology Rare | Phase 3 | 13 |
| OMER | OMEROS CORP | HematologyNeurologyOncologyRespiratory Rare | NDA Submitted | 7 |
| ORKA | Oruka Therapeutics, Inc. | DermatologyImmunology Rare | Phase 2 | 6 |
| OVID | Ovid Therapeutics Inc. | Neurology Rare | Phase 1 | 6 |
| KTTA | Pasithea Therapeutics Corp. | NeurologyOncology | Phase 1 | 3 |
| CATX | Perspective Therapeutics, Inc. | Oncology | Phase 1 | 3 |
| PHIO | Phio Pharmaceuticals Corp. | Oncology | Phase 1 | 4 |
| PMVP | PMV Pharmaceuticals, Inc. | Oncology | Phase 2 | 7 |
| PCSA | Processa Pharmaceuticals, Inc. | GI/HepatologyOncologyRenal Rare | Phase 2 | 8 |
| TARA | Protara Therapeutics, Inc. | DermatologyMetabolicOncology Rare | Phase 3 | 3 |
| REPL | Replimune Group, Inc. | Oncology | Phase 3 | 4 |
| RVPH | REVIVA PHARMACEUTICALS HOLDINGS, INC. | CardiovascularDermatologyNeurologyRespiratory Rare | Phase 3 | 10 |
| RYTM | RHYTHM PHARMACEUTICALS, INC. | Metabolic Rare | Approved | 13 |
| RCKT | ROCKET PHARMACEUTICALS, INC. | CardiovascularHematologyImmunology Rare | Approved | 4 |
| SGMT | Sagimet Biosciences Inc. | DermatologyMetabolic | Phase 3 | 5 |
| SANA | Sana Biotechnology, Inc. | MetabolicOncology | Phase 1 | 5 |
| SRPT | Sarepta Therapeutics, Inc. | Neurology Rare | Approved | 10 |
| SLS | SELLAS Life Sciences Group, Inc. | Oncology | Phase 3 | 8 |
| SLDB | Solid Biosciences Inc. | CardiovascularNeurology Rare | Phase 3 | 6 |
| SPRB | SPRUCE BIOSCIENCES, INC. | MetabolicNeurology Rare | Preclinical | 2 |
| SYRE | Spyre Therapeutics, Inc. | Immunology | Phase 2 | 12 |
| GPCR | Structure Therapeutics Inc. | MetabolicRespiratory Rare | Phase 2 | 5 |
| SMMT | Summit Therapeutics Inc. | Oncology | Phase 3 | 3 |
| STRO | SUTRO BIOPHARMA, INC. | Oncology | Phase 1 | 5 |
| TNGX | Tango Therapeutics, Inc. | Oncology | Phase 1 | 6 |
| TSHA | Taysha Gene Therapies, Inc. | Neurology Rare | Phase 3 | 3 |
| TVTX | Travere Therapeutics, Inc. | MetabolicRenal Rare | Approved | 4 |
| TTRX | Turn Therapeutics Inc. | DermatologyInfectious Disease | Phase 2 | 4 |
| RARE | Ultragenyx Pharmaceutical Inc. | CardiovascularGI/HepatologyMetabolicNeurology Rare | Approved | 12 |
| QURE | uniQure N.V. | HematologyMetabolicNeurology Rare | Approved | 6 |
| VNDA | Vanda Pharmaceuticals Inc. | CardiovascularDermatologyGI/HepatologyHematologyImmunologyInfectious DiseaseNeurologyOphthalmology Rare | Approved | 26 |
| VERA | Vera Therapeutics, Inc. | Infectious DiseaseRenal Rare | NDA Submitted | 8 |
| VKTX | Viking Therapeutics, Inc. | GI/HepatologyMetabolicNeurology Rare | Phase 3 | 9 |
| VIR | Vir Biotechnology, Inc. | Infectious DiseaseOncology Rare | Phase 3 | 10 |
| VRDN | Viridian Therapeutics, Inc.\DE | Ophthalmology | NDA Submitted | 6 |
| VOR | Vor Biopharma Inc. | ImmunologyNeurologyOncology Rare | Phase 3 | 4 |
| VYGR | Voyager Therapeutics, Inc. | MetabolicNeurology Rare | Phase 1 | 7 |
| VTVT | vTv Therapeutics Inc. | MetabolicRespiratory Rare | Phase 3 | 8 |
| WVE | Wave Life Sciences Ltd. | MetabolicNeurologyRespiratory Rare | Phase 2 | 5 |
| XENE | Xenon Pharmaceuticals Inc. | Neurology | Phase 3 | 9 |
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